Search Diseases

Diseases

UMLS CUI UMLS Term Proteins

C0700501

Congenital Nystagmus

AHR, ATF6

C0740340

Amyloidosis, Familial

FGA, TTR

C0745103

Hyperlipoproteinemia Type Iia

ABCA1, GHR, APOA2, LDLR

C0749794

Upper Extremity Deformities, Congenital

EZH2

C0751036

Hereditary Motor And Sensory Neuropathy Type I

PMP22

C0751038

Cockayne Syndrome, Type Ii

ERCC1

C0751039

Cockayne Syndrome, Type I

ERCC4

C0751083

Duane Retraction Syndrome, Type 2

CHN1

C0751156

Fraxa Syndrome

FMR1

C0751157

Fraxe Syndrome

AFF2, SERPINA1

C0751161

Udpglucose 4-Epimerase Deficiency Disease

GALE

C0751173

Glycogen Storage Disease Type Ii, Infantile

GAA

C0751202

Cystathionine Beta-Synthase Deficiency Disease

CBS

C0751208

Juvenile Huntington Disease

HTT

C0751273

Infantile Globoid Cell Leukodystrophy

GALC, PSAP

C0751276

Metachromatic Leukodystrophy, Juvenile Type

ARSA, PSAP

C0751278

Metachromatic Leukodystrophy, Infant

ARSA

C0751279

Metachromatic Leukodystrophy, Adult-Type (Disorder)

ARSA, PSAP

C0751336

Distal Muscular Dystrophies

TTN, MATR3

C0751337

X-Linked Emery-Dreifuss Muscular Dystrophy

EMD, FHL1

C0751383

Juvenile Neuronal Ceroid Lipofuscinosis

CLN3

C0751422

Hereditary Autoinflammatory Diseases

TNFAIP3

C0751617

Semilobar Holoprosencephaly

GAS1, GLI2, PTCH1, TDGF1, DISP1

C0751668

Machado-Joseph Disease Type I

ATXN3

C0751669

Machado-Joseph Disease Type Ii

ATXN3

C0751670

Machado-Joseph Disease Type Iii

ATXN3

C0751748

Nonketotic Hyperglycinemia

GCSH

C0751783

Lafora Disease

EPM2A

C0751785

Unverricht-Lundborg Syndrome

PRICKLE1, CSTB

C0751870

Heredodegenerative Disorders, Nervous System

CYGB, FTL, NGB

C0751915

Pelizaeus-Merzbacher Disease, Atypical

PLP1

C0751916

Classic Pelizaeus-Merzbacher Disease

PLP1

C0751917

Pelizaeus-Merzbacher Disease, Transitional

PLP1

C0752109

Brain Diseases, Metabolic, Inborn

FOLR1, NDUFAF2

C0752120

Spinocerebellar Ataxia Type 1

ATXN1

C0752160

Hemangioma, Cavernous, Central Nervous System

CCM2, KRIT1

C0752166

Bardet-Biedl Syndrome

SDCCAG8, IFT27, TTC8, BBS12, NPHP1, MKS1, BBS7, BBS1, BBS2, BBS10, MKKS, BBIP1

C0795907

Conotruncal Anomaly Face Syndrome

COMT, GP1BB, TBX1, HIRA, UFD1L

C0796147

Acrocallosal Syndrome

FOXG1, GLI3

C0848558

Hypospadias

MAMLD1, EXOC3, DGKK, GREM1, CCDC59, HOXA3, HSD3B2, KCNMA1, ZFHX3, ATF3, TAX1BP1

C0852077

Blood Coagulation Disorders, Inherited

MTHFR

C0878677

Glycogen Storage Disease Type Iib

LAMP2

C0878681

Dent'S Disease

CLCN5

C0917713

Becker Muscular Dystrophy

DMD

C0917715

Hajdu-Cheney Syndrome

NOTCH2

C0917796

Optic Atrophy, Hereditary, Leber

IL1A, IL1B

C0917817

Neurofibromatosis 3

NF2

C0936256

Lysine Alpha-Ketoglutarate Reductase Deficiency Disease

AASS

C0949116

Congenital Hypoplastic Anemia

UMPS, CAD

C0949595

Gonadal Dysgenesis, 46,Xx

FSHR, PSMC3IP, BMP15

C0949658

Cardiomyopathy, Hypertrophic, Familial

CRYAB, DES, DSG2, ANKRD1, LAMP2, TNNI3, TPM1, ACTN2, NEXN

C0950121

Denys-Drash Syndrome

WT1

C0950122

Frasier Syndrome

WT1

C1136249

Mental Retardation, X-Linked

PQBP1, RAB39B, PTCHD1, AGTR2, GDI1, MAOA, ATRX, PCDH19, SLC6A8, CASK

C1142166

Brugada Syndrome (Disorder)

TRPM4, CACNA1C, CACNA2D1, SLMAP

C1148551

X-Linked Dyskeratosis Congenita

DKC1

C1260899

Anemia, Diamond-Blackfan

RPL5, RPL11, RPL15, RPL26, RPL35A, RPS7, RPS10, RPS17, RPS26

C1264039

Von Willebrand Disease, Type 1

VWF

C1264040

Von Willebrand Disease, Type 2

VWF

C1264041

Von Willebrand Disease, Type 3

VWF

C1282968

Von Willebrand Disease, Type 2A

VWF

C1282971

Von Willebrand Disease, Type 2B

VWF

C1282974

Von Willebrand Disease Type 2M

VWF

C1282975

Von Willebrand Disease, Type 2N

VWF

C1306503

Congenital Exomphalos

CHRNA7, PCSK5

C1321489

Torre-Muir Syndrome

MSH6, MLH1, MSH2

C1328840

Autoimmune Lymphoproliferative Syndrome

FAS, NRAS, PRKCD, CASP8

C1333990

Hereditary Nonpolyposis Colorectal Cancer

MLH3, MSH6, KRAS, EPCAM, MLH1, MSH2, PIK3CA, PMS1, RPS20, BMPR1A, TGFBR2, LRRFIP2

C1333991

Hereditary Non-Polyposis Colon Cancer Type 2

MLH1

C1449843

Pseudohypoaldosteronism, Type I, Autosomal Recessive

SCNN1A, SCNN1G

C1449844

Pseudohypoaldosteronism, Type Ii

KLHL3, CUL3

C1450010

Plagiocephaly, Nonsynostotic

FGFR2

C1450051

Autosomal Recessive Emery-Dreifuss Muscular Dystrophy

LMNA

C1510455

Acrocephalosyndactylia

FGFR2, TWIST1

C1510460

Orofaciodigital Syndrome I

OFD1

C1527338

Hereditary Cerebral Amyloid Angiopathy, Icelandic Type

CST3

C1563719

Kallmann Syndrome 1

ANOS1

C1563720

Kallmann Syndrome 2 (Disorder)

FGFR1

C1567743

Alport Syndrome, Autosomal Dominant

COL4A3

C1567744

Alport Syndrome, Autosomal Recessive

COL4A3

C1568248

Usher Syndrome, Type Iii

HARS

C1621920

Intermediate Maple Syrup Urine Disease

PPM1K, DBT, BCKDHA, BCKDHB

C1704417

Hyperlipoproteinemia Type Iib

APOB

C1704429

Hypoalphalipoproteinemia, Familial

ABCA1, APOA1

C1706595

Pachyonychia Congenita, Jadassohn Lewandowsky Type

KRT16

C1720864

Sulfatidosis, Juvenile, Austin Type

SUMF1

C1720958

Hyper-Igm Immunodeficiency Syndrome, Type 5

UNG

C1720965

Ectodermal Dysplasia 3, Anhidrotic

EDARADD

C1721005

Leukokeratosis, Hereditary Mucosal

KRT13

C1721006

Keratoderma, Palmoplantar, Epidermolytic

KRT1, KRT9, KRT16

C1721007

Pachyonychia Congenita, Type 2 (Disorder)

KRT17

C1802395

Congenital Muscular Hypertrophy-Cerebral Syndrome

SMC1A

C1833340

Synostotic Posterior Plagiocephaly

ERF

C1836373

Muscular Dystrophy, Limb-Girdle, Type 2K

POMT1

C1836635

Loeys-Dietz Aortic Aneurysm Syndrome

TGFBR1

C1838244

Tibial Muscular Dystrophy, Tardive

TTN

C1839259

Bulbo-Spinal Atrophy, X-Linked

AR

C1845168

Hypophosphatemic Rickets, X-Linked Recessive

CLCN5

C1846545

Autoimmune Lymphoproliferative Syndrome Type 2B

CASP8

C1848201

Subcortical Band Heterotopia

EML1

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